Lentivirus vectors containing a miR-142-3p target sequence have been used to correct this disorder in mice.
Lentivirus vectors containing a miR-142-3p target sequence have been used to correct this disorder in mice. This disease may be caused by LINE transposon (*) insertion into a certain chromosome, and one effective treatment for this disease uses a protein extracted from Chinese hamster ovary cells. Arthropathy in sufferers of this disease can result from hemorrhage into joint spaces. The two types of this disease are caused by deficiencies of factor VIII and factor IX, which bind von Willebrand factor and are activated by thrombin. For 10 points, name this X-linked disorder in which blood does not clot sufficiently.
Lentivirus vectors containing a miR-142-3p target sequence have been used to correct this disorder in mice.
hemophilia